Blog & News - Page 2 of 3 - March

Blog & News

A Targeted Step Forward: Understanding WHIM Syndrome and a New Therapy

A Targeted Step Forward: Understanding WHIM Syndrome and a New Therapy

A New Horizon for Hemophilia B: Understanding the Journey of Gene Therapy.

A New Horizon for Hemophilia B: Understanding the Journey of Gene Therapy.

A Living Medicine: A New Chapter for Synovial Sarcoma

A Living Medicine: A New Chapter for Synovial Sarcoma

Targeting Rare Diseases: The Power of In Vivo Base Editing

Targeting Rare Diseases: The Power of In Vivo Base Editing

A Journey into the Cell: Understanding LSDs and Enzyme Replacement Therapy

A Journey into the Cell: Understanding LSDs and Enzyme Replacement Therapy

When Passion Meets Possibility: Insights from March’s AI x Rare Disease Event

When Passion Meets Possibility: Insights from March’s AI x Rare Disease Event

Beyond “Rare”: Rethinking the Diagnostic Odyssey at our GenAI x rare disease event

Beyond “Rare”: Rethinking the Diagnostic Odyssey at our GenAI x rare disease event

Getting to know Dr. Sadaf Ashtari and her 15-Year Journey to Rare Disease Diagnosis

Blog Interviews

Getting to know Dr. Sadaf Ashtari and her 15-Year Journey to Rare Disease Diagnosis

Potentials of Generative AI to Empower Rare Disease Communities

Potentials of Generative AI to Empower Rare Disease Communities

Getting to Know JC Muyl: The Founder of MyRareData

Getting to Know JC Muyl: The Founder of MyRareData

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